Beam Therapeutics gave an initial look at the first handful of patients who received its experimental gene-edited treatment for sickle cell disease.
Beam has adopted a similar trial design to the studies that supported the approvals of Casgevy and bluebird bio’s Lyfgenia. The precedents suggest Beam could win approval with data on 30 patients.
A patient with sickle cell disease died while participating in a clinical trial of a CRISPR-based treatment from Beam Therapeutics, threatening to overshadow early signals of effective gene editing.
Department of Biomedical Engineering, Texas A&M University, College Station, Texas 77843, United States Electrical & Computer Engineering Department, University of California, Los Angeles, California ...
Israel's "Iron Beam," a laser defense system to counter missiles, drones, and other aerial threats, is set to become operational next year. Developed alongside the Iron Dome, this innovative ...
One of the main connections between Cincinnati and Northern Kentucky could be closed for weeks after a fire under the Daniel Carter Beard Bridge damaged its steel structure, officials said Friday.
During the maneuvers the US Marines fully operated the Iron Dome system including intercepting targets. In addition, the continuous launch capability of Iron Dome interceptors from a mobile launcher, ...