RNA editing is the next frontier in gene therapy—here's what you need to know
The United States Food and Drug Administration has just approved the first-ever clinical trial that uses CRISPR-Cas13 RNA ...
Medpage Today on MSN12 天
Novel CRISPR-Cas9-Based Promising in ATTR Cardiomyopathy
A CRISPR-Cas9-based investigational therapy was linked with a drop in serum transthyretin (TTR) levels in patients with ...
News Medical on MSN2 天
First U.S. trial uses non-viral CRISPR to correct sickle cell mutation
UCSF Benioff Children's Hospital Oakland is enrolling patients in an innovative clinical trial that seeks to cure sickle cell ...
UC San Francisco6 天
Novel Gene Therapy Trial for Sickle Cell Disease Launches
UCSF Benioff Children’s Hospital Oakland is enrolling patients in an innovative clinical trial that seeks to cure sickle cell ...
Frontiers22 天
CRISPR/Cas9 in Cancer: Pioneering Gene Editing for Enhanced Drug Discovery
This underscores the critical need for novel therapeutic strategies that can effectively control and potentially reverse carcinogenesis. This Research Topic is centered on CRISPR-Cas9, a ...
Crispr Therapeutics Q3 Earnings: No Casgevy Revenue, But Plenty Of Optimism
Crispr has already secured a historic first approval for a CRISPR/Cas9 drug and has several more potential blockbuster ...