Kanglin Biotech is a China based company, focusing on the research, development and commercialization of first-in-class and best-in-class gene therapy drugs, most of which are targeted at diseases ...

Investigators said patients experienced adverse effects in line with those expected for myeloablative conditioning with ...

UCSF Benioff Children's Hospital Oakland is enrolling patients in an innovative clinical trial that seeks to cure sickle cell ...

UCSF Benioff Children’s Hospital Oakland is enrolling patients in an innovative clinical trial that seeks to cure sickle cell ...

Oct. 28, 2024 — Using state-of-the-art technology, researchers have identified several specific steps needed for CRISPR to become active and perform its gene editing function. These preclinical ...

Nov. 25, 2024 — A groundbreaking method to profile gene activity in the living human brain has been developed. This innovative approach opens new avenues for understanding and treating ...

The therapy – which is based on CD34+ stem cells taken from patients that are modified to carry a working gene for beta-globin, a haemoglobin component that is deficient in thalassemia patients ...

Gene therapy involves the introduction of new genes into cells, to restore or add gene expression, for the purpose of treating disease. Most commonly a mutated gene is replaced with DNA encoding a ...

Gene regulation refers to the mechanisms that act to induce or repress the expression of a gene. These include structural and chemical changes to the genetic material, binding of proteins to ...

Eye color is a complex genetic trait determined by pairings of genes passed on from each parent. Scientists once believed eye color was determined by a single gene, but advances in genetic research ...

Genetic disorders are diseases caused by an abnormal gene, often described as a mutation. When such diseases are inherited (rather than the result of a random mutation), it means they are passed along ...